Artemis splice defects cause atypical SCID and can be restored in vitro by an antisense oligonucleotide
- Ijspeert, H.
- Lankester, A.C.
- Van Den Berg, J.M.
- Wiegant, W.
- Van Zelm, M.C.
- Weemaes, C.M.R.
- Warris, A.
- Pan-Hammarström, Q.
- Pastink, A.
- Van Tol, M.J.D.
- Van Dongen, J.J.M.
- Van Gent, D.C.
- Van Der Burg, M.
ISSN: 1466-4879, 1476-5470
Year of publication: 2011
Volume: 12
Issue: 6
Pages: 434-444
Type: Article